Discover how bone marrow delivery of genetically modified CD34+ HSPCs improves homing and engraftment of short-term progenitors over long-term repopulating hematopoietic stem cells.
Exploring the latest advances in transfusion therapy, pharmacological treatments, and groundbreaking gene therapies for sickle cell disease.
Explore how French researchers are advancing genome editing technologies for gene therapy applications, tackling genetic disorders with innovative CRISPR-based approaches.
Explore how adenovirus-delivered CRISPR/Cas9 gene editing technology is revolutionizing HIV treatment by targeting the CCR5 receptor.
Explore how lipid nanoparticles are transforming gene therapy, enabling safe DNA delivery and targeted treatments for chronic diseases like diabetes, cancer, and heart conditions.
How CRISPR gene editing and advanced gene therapies are transforming veterinary oncology by targeting cancer at its genetic roots.
Exploring how CRISPR gene editing challenges traditional distinctions between therapy and enhancement through groundbreaking medical cases.
Explore how CRISPR gene editing is transforming the treatment of inherited blindness through groundbreaking clinical trials and innovative therapies.
Explore how CRISPR-Cas9 is transforming hematology, from curing sickle cell disease to personalized gene therapies for rare blood disorders.
How CRISPR/Cas9 gene-editing technology offers hope for curing Duchenne Muscular Dystrophy by correcting the root genetic cause of this devastating disorder.